Hereditary Central Nervous System Demyelinating Diseases - 25 Studies Found
Recruiting |
: Biomarker for Metachromatic Leukodystrophy Disease :
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Recruiting |
: Aclarubicin for the Treatment of Retinal Vasculopathy With Cerebral Leukodystrophy :
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Terminated |
: Natural History Study of Children With Metachromatic Leukodystrophy :
: 2011-08-29 |
Recruiting |
: Krabbe Disease Global Patient Registry : Krabbe Disease : 2016-12-06 |
Recruiting |
: A Natural History Study of Canavan Disease : Canavan Disease : 2016-07-28 |
Recruiting |
: Natural History and Outcome Measures in Alexander Disease : Alexander Disease : 2016-02-19 |
Recruiting |
: Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy :
: 2015-08-12 : Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f |
No longer available |
: Single Patient Expanded Access Protocol: Metabolic Boost : Metachromatic Leukodystrophy : 2013-12-19 : Biological: Enriched Hematopoetic Stem Cell Infusion Enriched Hematopoetic Stem Cell Infusion |
Enrolling by invitation |
: Open-Label Extension Study Evaluating Safety and Efficacy of HGT-1110 in Patients With Metachromatic Leukodystrophy : Metachromatic Leukodystrophy (MLD) : 2013-06-20 :
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